UPCOMING CONFERENCE

Scientific Program

UPCOMING CONFERENCE

Scientific Program

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Link to current page: https://www.jain-foundation.org/8th-dysferlin-conference/scientific-program

EIGHTH DYSFERLIN CONFERENCE

Speaker Sessions I-VIII: Ballroom C

Reception: Upper Pool Deck

Poster Session I & II: Ballroom D

Breakfast & Lunch: Ballroom D

WEDNESDAY, March 11

 

 

Registration

12:00 – 2:00 PM

 

 

Welcome – Laura Rufibach

2:00 – 2:10 PM

Session I: Clinical Outcomes in Dysferlinopathy

2:10 – 3:45 PM 

Introduction – Laura Rufibach
Volker Straub (45 min) Anna Mayhew (25 min)

 

 

Break

3:45 – 4:15 PM

 

Session II: New Developments in Dysferlinopathy

4:15 – 6:30 PM 

Introduction – Brad Williams

Matthew Watt (25 min), Jyoti Jaiswal (25 min), Alistair Khodabukus (25 min),
Elizabeth McNally (25 min)

 

 

Reception

7:00 – 9:00 PM

 

THURSDAY, March 12

 

Breakfast

7:00 – 8:00 AM

 

Session III: Potential Therapeutics

8:00 – 9:45 AM

Introduction – Laura Rufibach
Alexis Demonbreun (25 min), Pam VanRy (25 min)
Monkol Lek (10 min), Matt Hirsch (10 min)

 

Patient Perspective –

9:45 – 10:00 AM

 

Break

10:00 – 10:30 AM

 

Session III: Potential Therapeutics continued

10:30 – 12:15 PM

Mohan Viswanathan (25 min), Luis Cea (25 min)
Rika Maruyama (10 min), Kevin Sonnemann (10 min)

 

 

Jain Foundation Initiatives: Preclinical Trials – Doug Albrecht

12:15 – 12:45 PM

 

Lunch

12:45 – 1:45 PM

 

Session IV: Dysferlin and Lipids

1:45 – 3:45 PM

Introduction – Brad Williams
Pascal Bernatchez (25 min), Lorenzo Puri (10 min), Pierre Carlier (25 min)
Anil Agarwal (10 min), Zoe White (10 min)

 

Patient Perspective –

3:45 – 4:00 PM

 

Poster Session I

4:00 – 6:30 PM

 

Gala Dinner

7:00 – 9:00 PM

 

FRIDAY, March 13

 

Breakfast

7:00 – 8:00 AM

 

Session V: Dysferlin Function

8:00 – 9:45 AM

Introduction – Doug Albrecht
Dennis Drescher and Marian Drescher (35 min), Aldo Meizoso-Huesca (10 min),
Miranda Grounds (10 min), Frances Lemckert (10 min)

 

 

Break

9:45 – 10:15 AM

 

Session V: Dysferlin Function continued

10:15 – 12:30 PM

Robert Bloch and Noah Weisleder (35 min), Elizabeth Barton (25 min),
Erin Lloyd (10 min), Christina Pacak (10 min)

 

 

 

Jain Foundation Initiatives: Patient Programs

12:30 – 1:00 PM

 

 

Lunch

1:00 – 2:00 PM

 

 

Session VI: Evaluating Patients

2:00 – 3:45 PM

Introduction – Sarah Emmons
Harmen Reyngoudt (10 min), Meredith James (10 min),
Joshua Zimmerberg (10 min), Samya Chakravorty (10 min),
Patient experience with COS (20 min)

 

 

Patient Perspective –

3:45 – 4:00 PM

 

 

Poster Session II

4:00 – 6:30 PM

 

 

SATURDAY, March 14

 

 

Breakfast and Hotel Check Out

7:00 – 8:00 AM

 

 

Session VII: Dysferlin and the Immune System

8:00 – 9:45 AM

Introduction – Doug Albrecht

Connie Jackaman (25 min), Noah Weisleder (25 min), Timothy Koh (10 min),
Juan-Carlos Saez (10 min)

 

 

Patient Perspective –

9:45 – 10:00 AM

 

Break

10:00 – 10:30 AM

 

Session VIII: Dysferlin Structure/Function

10:30 – 12:00 PM

Introduction – Brad Williams

Mike Rout (25 min), Bryan Sutton (25 min), Colin Johnson (10 min)

 

 

Closing Remarks

12:00 – 12:30 PM