DYSFERLIN CONFERENCE
Scientific Program
DYSFERLIN CONFERENCE
Scientific Program
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Jain Foundation 2024 Dysferlin Conference Agenda
May 8-11, 2024, Houston, TX
| WEDNESDAY, May 8 | ||||
| Registration | 12:00 | – | 2:00 PM | |
| Welcome | 2:00 | – | 2:10 PM | |
| Session I: Clinical Studies | 2:10 | – | 4:45 PM | |
| Introduction Volker Straub (25 min), Meredith James (25 min) Harmen Reyngoudt (25 min), Mary Neal (10 min), Ana Topf (10 min), Young Jae Moon (10 min) |
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| Break | 4:45 | – | 5:15 PM |
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| Session II: Featured Topics | 5:15 | – | 7:00 PM | |
| Introduction Nenad Bursac (25 min), Bryan Sutton (25 min), Chiara Nicoletti (10 min),Karim Ismat (10 min) |
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| Reception | 7:00 | – | 9:00 PM | |
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THURSDAY, May 9 |
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| Breakfast | 7:30 | – | 8:30 AM | |
| Session III: Genetic Therapies | 8:30 | – | 10:15 AM | |
| Introduction Oliver Rogers – Sarepta (25 min), Doug Anderson – SCRIPTr (25 min), Camille Bouchard (10 min), Joe Yasa (10 min) |
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| Break | 10:15 | – | 10:45 AM | |
| Session IV: Lipids/Cholesterol | 10:45 | – | 12:45 PM | |
| Introduction Pascal Bernatchez (25 min), Alastair Khodabukus (25 min), Stacey Keenan (10 min), Bradley Launikonis (10 min), Zeren Sun (10 min) |
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| Lunch | 12:45 | – | 1:45 PM | |
| Jain Foundation Initiatives | 1:45 | – | 2:15 PM | |
| Session V: Potential Therapeutics I | 2:15 | – | 4:00 PM | |
| Introduction Julio Cesar Cardenas (25 min) Regula Furrer (10 min), Noah Weisleder (10 min) Matthew Watt (25 min) |
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| Poster Session | 4:00 | – | 7:00 PM | |
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FRIDAY, May 10 |
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| Breakfast | 7:30 | – | 8:30 AM | |
| Session VI: Potential Therapeutics II | 8:30 | – | 10:15 AM | |
| Introduction Mohan Viswanathan (25 min), Pam Van Ry (25 min), Valeria Agostini (10 min), Gianni Giarrano (10 min) |
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| Break | 10:15 | – | 10:45 AM | |
| Session VII: Dysferlin and Calcium Handling | 10:45 | – | 12:30 PM | |
| Introduction Robert Bloch (35 min), Aldo Meizoso Huesca (25 min), Callum Jay Quinn (10 min) |
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| Jain Foundation Initiatives | 12:30 | – | 1:00 PM | |
| Lunch | 1:00 | – | 2:00 PM | |
| Session VIII: Dysferlin and the Immune System | 2:00 | – | 3:00 PM | |
| Introduction Noah Weisleder (25 min), Lelinh Duong (10 min) |
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| Real World Perspectives and Insights from Community Members: A Workshop for Connection |
3:00 | – | 4:00 PM | |
| Session VIII: Dysferlin and the Immune System (cont.) | 4:00 | – | 4:45 PM | |
| Connie Jackaman (35 min) | ||||
| Prepare for dinner (meet in lobby at 6pm to catch buses) |
5:00 | – | 6:30 PM | |
| Gala Dinner at the Natural History Museum | 6:30 | – | 10:00 PM | |
| . SATURDAY, May 11 |
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| Breakfast and Hotel Check Out | 7:30 | – | 8:30 AM | |
| Session IX: Dysferlin – New Insights | 8:30 | – | 10:45 AM | |
| Introduction Robyn Murphy (25 min), Stefan Wette (10 min), Miranda Grounds (25 min),Hannah Bulgart (25 min), Peter Fridy (10 min) |
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| Break | 10:45 | – | 11:15 AM | |
| Conclusions and Next Steps (Interactive Discussion/Brainstorming) |
11:15 | – | 11:45 AM | |
| Closing Remarks | 11:45 | – | 12:00 PM | |















