UPCOMING CONFERENCE
Scientific Program
UPCOMING CONFERENCE
Scientific Program
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Link to current page: https://www.jain-foundation.org/8th-dysferlin-conference/scientific-program
EIGHTH DYSFERLIN CONFERENCE
Speaker Sessions I-VIII: Ballroom C
Reception: Upper Pool Deck
Poster Session I & II: Ballroom D
Breakfast & Lunch: Ballroom D
WEDNESDAY, March 11
Registration
12:00 – 2:00 PM
Welcome – Laura Rufibach
2:00 – 2:10 PM
Session I: Clinical Outcomes in Dysferlinopathy
2:10 – 3:45 PM
Introduction – Laura Rufibach
Volker Straub (45 min) Anna Mayhew (25 min)
Break
3:45 – 4:15 PM
Session II: New Developments in Dysferlinopathy
4:15 – 6:30 PM
Introduction – Brad Williams
Matthew Watt (25 min), Jyoti Jaiswal (25 min), Alistair Khodabukus (25 min),
Elizabeth McNally (25 min)
Reception
7:00 – 9:00 PM
THURSDAY, March 12
Breakfast
7:00 – 8:00 AM
Session III: Potential Therapeutics
8:00 – 9:45 AM
Introduction – Laura Rufibach
Alexis Demonbreun (25 min), Pam VanRy (25 min)
Monkol Lek (10 min), Matt Hirsch (10 min)
Patient Perspective –
9:45 – 10:00 AM
Break
10:00 – 10:30 AM
Session III: Potential Therapeutics continued
10:30 – 12:15 PM
Mohan Viswanathan (25 min), Luis Cea (25 min)
Rika Maruyama (10 min), Kevin Sonnemann (10 min)
Jain Foundation Initiatives: Preclinical Trials – Doug Albrecht
12:15 – 12:45 PM
Lunch
12:45 – 1:45 PM
Session IV: Dysferlin and Lipids
1:45 – 3:45 PM
Introduction – Brad Williams
Pascal Bernatchez (25 min), Lorenzo Puri (10 min), Pierre Carlier (25 min)
Anil Agarwal (10 min), Zoe White (10 min)
Patient Perspective –
3:45 – 4:00 PM
Poster Session I
4:00 – 6:30 PM
Gala Dinner
7:00 – 9:00 PM
FRIDAY, March 13
Breakfast
7:00 – 8:00 AM
Session V: Dysferlin Function
8:00 – 9:45 AM
Introduction – Doug Albrecht
Dennis Drescher and Marian Drescher (35 min), Aldo Meizoso-Huesca (10 min),
Miranda Grounds (10 min), Frances Lemckert (10 min)
Break
9:45 – 10:15 AM
Session V: Dysferlin Function continued
10:15 – 12:30 PM
Robert Bloch and Noah Weisleder (35 min), Elizabeth Barton (25 min),
Erin Lloyd (10 min), Christina Pacak (10 min)
Jain Foundation Initiatives: Patient Programs
12:30 – 1:00 PM
Lunch
1:00 – 2:00 PM
Session VI: Evaluating Patients
2:00 – 3:45 PM
Introduction – Sarah Emmons
Harmen Reyngoudt (10 min), Meredith James (10 min),
Joshua Zimmerberg (10 min), Samya Chakravorty (10 min),
Patient experience with COS (20 min)
Patient Perspective –
3:45 – 4:00 PM
Poster Session II
4:00 – 6:30 PM
SATURDAY, March 14
Breakfast and Hotel Check Out
7:00 – 8:00 AM
Session VII: Dysferlin and the Immune System
8:00 – 9:45 AM
Introduction – Doug Albrecht
Connie Jackaman (25 min), Noah Weisleder (25 min), Timothy Koh (10 min),
Juan-Carlos Saez (10 min)
Patient Perspective –
9:45 – 10:00 AM
Break
10:00 – 10:30 AM
Session VIII: Dysferlin Structure/Function
10:30 – 12:00 PM
Introduction – Brad Williams
Mike Rout (25 min), Bryan Sutton (25 min), Colin Johnson (10 min)
Closing Remarks
12:00 – 12:30 PM